Monthly Archives: August 2022

17 Days of September

Posted on August 31, 2022 by melelllan

Tomorrow is not a day like any other day. Tomorrow is the first day of the last 17 days of the last month of the last year before we know if Trofinetide is going to get its shot. It could … Continue reading →

Posted in Acadia, FDA, hope, Trail to a Texas Trial, Trofinetide | Leave a comment

Where do we go From Here? Part I

Posted on August 10, 2022 by melelllan

Last week, the International Rett syndrome Foundation (IRSF) held a webinar with Dr. Dominique Pichard, CSO, IRSF and Mr. James E. Valentine, Esq., HPM aptly named, “What Comes Next? The FDA Regulatory Process from NDA to FDA decision and beyond.” … Continue reading →

Posted in Acadia, clinicaltrials.gov, Dame Margaret Brimble, FDA, International Rett syndrome Foundation, Intrepid 2566, LAVENDER TRIAL, Neuren Pharmaceuticals, NNZ-2566, NNZ-2566 trial, orphan drug designation, Rett Research, Rett Syndrome, rettsyndrome.org, TBI, Trail to a Texas Trial, Trofinetide Pediatric trial, Trofinetide Phase III | Tagged , , , , , , , | Leave a comment