Category Archives: Orpan Drug Status

The Next Steps Through the Desert

Wow. While time has been passing, Neuren has quietly, behind the scenes, ¬†been taking step after step and gaining ground with Trofinetide. Check out their latest announcements… http://www.neurenpharma.com/IRM/ShowDownloadDoc.aspx?SiteId=386&AnnounceGuid=23a3caf0-969f-4269-824e-fe32548eefa9 http://www.neurenpharma.com/IRM/ShowDownloadDoc.aspx?SiteId=386&AnnounceGuid=89e7ec87-31e5-4aa3-b029-0b449df3189c So, to me it feels like we went from full stop … Continue reading

Posted in Congress, cure, Neuren Pharmaceuticals, Orpan Drug Status, Rett Research, Rett Syndrome, rettsyndrome.org, Trail to a Texas Trial, Trofinetide | Tagged , , , , , , | Leave a comment

It’s Official!

This morning Neuren released a statement in regards to Orphan Drug Status for Trofinetide (NNZ 2566) See their announcement here. They’ve also come out with an awesome video about the science behind Trofinetide. Take a look! Great graphics and pretty … Continue reading

Posted in FDA, Neuren Pharmaceuticals, NNZ-2566, Orpan Drug Status, Trofinetide | Tagged , , , , , , | Leave a comment