Category Archives: Orpan Drug Status

The Next Steps Through the Desert

Wow. While time has been passing, Neuren has quietly, behind the scenes,  been taking step after step and gaining ground with Trofinetide. Check out their latest announcements… So, to me it feels like we went from full stop … Continue reading

Posted in Congress, cure, Neuren Pharmaceuticals, Orpan Drug Status, Rett Research, Rett Syndrome,, Trail to a Texas Trial, Trofinetide | Tagged , , , , , , | Leave a comment

It’s Official!

This morning Neuren released a statement in regards to Orphan Drug Status for Trofinetide (NNZ 2566) See their announcement here. They’ve also come out with an awesome video about the science behind Trofinetide. Take a look! Great graphics and pretty … Continue reading

Posted in FDA, Neuren Pharmaceuticals, NNZ-2566, Orpan Drug Status, Trofinetide | Tagged , , , , , , | Leave a comment